Search for Clinical Trial Results

Mucopolysaccharidosis Type I - 5 Studies Found
Status | Study |
Enrolling by invitation |
Study Name: Immunodeficiency in Cartilage-hair Hypoplasia: Sub-project on Safety of Vaccination Against Chickenpox Condition: Date: 2025-03-19 |
Recruiting |
Study Name: Safety and Dose Ranging Study of Insulin Receptor MoAb-IDS Fusion Protein in Patients With Hunter Syndrome Condition: Date: 2025-03-19 |
Active, not recruiting |
Study Name: Study of Intrathecal Idursulfase-IT Administered in Conjunction With Elaprase® in Pediatric Patients With Hunter Syndrome and Early Cognitive Impairment Condition: Date: 2025-03-19 |
Enrolling by invitation |
Study Name: Ultrasound Findings of Finger, Wrist and Knee Joints in Mucopolysaccharidosis Condition:
Date: 2013-08-13 |
Completed |
Study Name: Study of DNL126 in Pediatric Participants With Mucopolysaccharidosis Type IIIA (Sanfilippo Syndrome Type A) Condition: Mucopolysaccharidosis Type IIIA Date: 2025-03-19 Interventions: intravenous repeating dose |