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Krabbe Disease - 1 Studies Found
| Status | Study |
| Completed |
Study Name: Gene Transfer Clinical Trial for Infantile and Late Infantile Krabbe Disease Treated Previously With HSCT Condition: Krabbe Disease Date: 2025-04-22 Interventions: A replication-deficient adeno-associated virus gene transfer vector expressing the human galactocerebrosidase (GALC) cDNA will be delivered one-time t |